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  Events - October 2012

SMi's Orphan Drugs and Rare Diseases

08 Oct 2012 - 09 Oct 2012 - London, UK

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SMi present…

Orphan Drugs & Rare Diseases

Innovative strategies for getting orphan drugs to where they are needed...

8th & 9th October 2012, The Copthorne Tara Hotel, London, UK

The call to treat rare diseases has become increasingly greater around the world than ever before. Supportive organisations including patient groups, national health authorities, health trusts, academia, HTAs, pharmaceutical and biotechnical companies are now progressively growing in numbers and sophistication in their approaches to medicinal care for those with rare and ultra-rare diseases.  

SMi’s Orphan Drugs & Rare Diseases conference will present briefings from key opinion leaders, those with hands-on experience of regulating new drug discoveries, companies that have already developed advanced orphan drugs & successfully been granted orphan medicine status and selected experts in the field.  Our expert speakers will offer unique insights into cutting-edge international developments taking place in: expanding the reach of medicine to previously untreatable and unreachable patients with rare diseases; different regulatory and policy environments; new drug discoveries; innovative business strategies & funding & financing models, and the importance of partnerships with patient groups and those at the point-of-care.   

Reasons why you should attend:

Foster better partnerships across sectors to develop orphan medicines

Secure more sources of funding to finance research and development

Gain competitive market access insights

Apply better business strategies and economic models for pricing and reimbursement requirements

Critically assess new developments in small molecule and gene therapy

Quote “Technology Network” and save £100

Register online here:

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